The cell and gene therapy CDMO market is experiencing significant growth, driven by the increasing number of cell and gene therapy candidates advancing through clinical development and ...

The U.S. Ophthalmic Clinical Trials Market was valued at USD 0.66 Billion in 2025 and is projected to reach USD 1.25 Billion by 2035, while Europe is expected to grow from USD 0.49 Billion to USD 0.89 ...

How do you approach clinical trial design for cell and gene therapies? There are a lot of similarities, but also some notable differences that I have encountered the last 15 years working in multiple ...

Developed in collaboration with Korea's top clinical and hospital network, the integrated platform combines globally ...

The treatment, administered at Schneider Children’s Medical Center of Israel in Petah Tikva, is a major milestone in the ...

Academic medical centers must play a crucial part in overcoming cell and gene therapy development hurdles by establishing institutional frameworks that offer comprehensive support extending beyond ...

An eight-month-old infant with a severe genetic epilepsy has become the first patient in the world to receive an experimental gene replacement therapy designed to restore the function of the WWOX gene ...

Rett syndrome is a devastating rare and progressive neurodevelopmental disease with high unmet need and a profound lifelong burden for patients and caregivers. It is well characterized clinically ...

Regenxbio Inc. RGNX on Monday said it aligned with the Food and Drug Administration (FDA) regarding the next steps needed for ...

Challenges in the development of treatments for hereditary hearing loss include the exploration of the underlying pathological mechanisms, the comprehensive evaluation of safety and efficacy of gene ...

Quality by design is critical for cell and gene therapy manufacturing where process controls directly influence product ...

An 8-month-old infant with severe genetic epilepsy has become the first patient in the world to receive an experimental gene ...